A rare disease is any disease that affects only a selected portion of its natural population. In some regions of the globe, a rare disease is simply a rare disease whose scarcity means that a business generating pharmaceuticals from that resource has little to no demand. There are two major categories of rare diseases namely infectious and non-infectious. An infectious disease is one in which an organism is passed from person to person through contact with the infected substance There are also a number of organizations and foundations that aim to find rare disease drugs. It is an enormous effort, taking into account the small number of cases involved. Many pharmaceutical companies have formed foundations and research foundations for rare diseases.
Another example of rare diseases is cystic fibrosis. It is caused by a genetic abnormality where the pancreas does not produce enough insulin. This results in excessive fat being produced in the pancreas, and the resulting condition is life-threatening. However, since there are a small number of people with this condition, there are not as many drugs to treat it. As a result, many scientists are trying to find ways to develop medicines that will specifically cure people suffering from this condition.
An example of a very rare disease that only affects a very small population is the rare disease called the AIDS orphan disease. This disease was caused by the HIV virus, which is transmitted through sexual contact. AIDS is a fatal disease and also can cause other problems such as blood poisoning and other life-threatening conditions. Unlike most other diseases, AIDS is also a transmittable disease meaning it can spread from one person to another once it has taken hold. Recently, the U.S. Food and Drug Administration (FDA) granted approval for a rare disease drugs called BCX9930 by BioCryst Pharmaceuticals, Inc. indicated for the treatment of paroxysmal nocturnal hemoglobinuria (PNH).
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